Synonyms
1-deoxygalactonojirimycin
(2R,3S,4R,5S)-2-(hydroxymethyl)piperidine-3,4,5-triol
DDIG
Description
Migalastat is pharmacologic chaperone of alpha-galactosidase the intrahepatic enzyme that is deficient in Fabry disease. Clinical experience with migalastat is limited, but it not been linked to serum enzyme elevations during therapy or to instances of clinically apparent acute liver injury.